Global Rare Disease Treatment Market Outlook, Trends And Future Opportunities (2023-2030)

Global Rare Disease Treatment Market Outlook, Trends And Future Opportunities (2023-2030)

Global Rare Disease Treatment Market, Treatment Type (Biologics, Biosimilar, Others), Therapy Area (Oncology, Neurological Diseases, Cardiovascular Diseases, Infectious Diseases, Musculoskeletal Diseases, Hematologic Diseases, Others), Route of Administration (Oral, Injectable, Others), Distribution Channel (Hospital Pharmacies, Specialty Pharmacies, Online Pharmacies), Region (North America, Europe, Asia Pacific, Latin America, Middle East & Africa) The report offers a comprehensive view of the market from supply as well as demand side to help take informed decisions.

  • Published On: Sep 2023
  • Report ID: IDA39
  • Region: Global
  • Format: PDF/EXCEL

Section 1. Report Objective, and Methodology

  • Scope of Research
  • Research Methodology
  • Assumptions
  • Research Sources
    • Primary Research
    • Secondary Research
    • Paid Databases

Section 2. Report Summary

  • Global Market Snapshot, 2022-2030
  • Executive Summary by Segments
    • Market Overview, By Treatment Type
    • Market Overview, By Therapy Area
    • Market Overview, By Route of Administration
    • Market Overview, By Distribution Channel
    • Market Overview, By Region

Section 3. Key Insights

  • Market Dynamics
    • Market Drivers
    • Market Restraints
    • Market Opportunities
  • Key Developments
  • Leading Brands
  • Price Trend Analysis
  • Pipeline Analysis
  • Porter’s Analysis
  • Epidemiology
  • Technology Insights
  • Impact of COVID-19

Section 4. Global Rare Disease Treatment Market, By Treatment Type, Market Size, and Revenue Opportunity (USD Billion, 2022-2030)  

  • Global Industry Overview, By Treatment Type
    • Market Size, US$ Bn
    • Market Share Analysis, 2022 and 2030 (%)
    • Market Trends and Dynamics
  • Biologics (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
  • Biosimilars (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
  • Others (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))

Section 5. Global Rare Disease Treatment Market, By Therapy Area, Market Size, and Revenue Opportunity (USD Billion, 2022-2030)  

  • Global Industry Overview, By Therapy Area
    • Market Size, US$ Bn
    • Market Share Analysis, 2022 and 2030 (%)
    • Market Trends and Dynamics
  • Oncology (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
  • Neurological Diseases (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
  • Cardiovascular Diseases (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
  • Infectious Diseases (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
  • Musculoskeletal Diseases (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
  • Hematologic Diseases (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
  • Others (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))

Section 6. Global Rare Disease Treatment Market, By Route of Administration, Market Size, and Revenue Opportunity (USD Billion, 2022-2030)

  • Global Industry Overview, By Therapy Area
    • Market Size, US$ Bn
    • Market Share Analysis, 2022 and 2030 (%)
    • Market Trends and Dynamics
  • Oral (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
  • Injectable (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
  • Others (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))

Section 7. Global Rare Disease Treatment Market By Distribution Channel, Market Size, and Revenue Opportunity (USD Billion, 2022-2030)

  • Global Industry Overview, By Distribution Channel
    • Market Size, US$ Bn
    • Market Share Analysis, 2022 and 2030 (%)
    • Market Trends and Dynamics
  • Hospital Pharmacies (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
  • Specialty Pharmacies (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
  • Online Pharmacies (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))

Section 8. Global Rare Disease Treatment Market By Region, Market Size, and Revenue Opportunity (USD Billion, 2022-2030)

  • Global Industry Overview, By Distribution Channel
    • Market Size, US$ Bn
    • Market Share Analysis, 2022 and 2030 (%)
    • Market Trends and Dynamics
  • North America
    • By Treatment Type (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
    • By Therapy Area (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
    • By Route of Administration (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
    • By Distribution Channel (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
    • By Country (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
      • U.S.
      • Canada
  • Latin America
    • By Treatment Type (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
    • By Therapy Area (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
    • By Route of Administration (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
    • By Distribution Channel (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
    • By Country (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
      • Brazil
      • Mexico
      • Rest of Latin America
  • Europe
    • By Treatment Type (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
    • By Therapy Area (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
    • By Route of Administration (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
    • By Distribution Channel (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
    • By Country (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
      • Germany
      • U.K.
      • France
      • Italy
      • Spain
      • Rest of Europe
  • Asia Pacific
    • By Treatment Type (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
    • By Therapy Area (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
    • By Route of Administration (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
    • By Distribution Channel (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
    • By Country (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
      • China
      • Japan
      • South Korea
      • India
      • ASEAN
      • Rest of APAC
  • Middle East and Africa
    • By Treatment Type (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
    • By Therapy Area (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
    • By Route of Administration (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
    • By Distribution Channel (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
    • By Country (Market Size and Forecast, and Y-o-Y Growth, 2022–2030, (US$ Billion))
      • Saudi Arabia
      • UAE
      • Rest of MEA

Section 9.  Company Profiles                    

  • F. Hoffmann-La Roche Ltd.
    • Company Overview
    • Product Portfolio and Performance
    • Financial Performance
    • Technology Insights
    • Strategic Initiatives
  • Pfizer, Inc.
    • Company Overview
    • Product Portfolio and Performance
    • Financial Performance
    • Technology Insights
    • Strategic Initiatives
  • PTC Therapeutics
    • Company Overview
    • Product Portfolio and Performance
    • Financial Performance
    • Technology Insights
    • Strategic Initiatives
  • AstraZeneca
    • Company Overview
    • Product Portfolio and Performance
    • Financial Performance
    • Technology Insights
    • Strategic Initiatives
  • Novartis AG
    • Company Overview
    • Product Portfolio and Performance
    • Financial Performance
    • Technology Insights
    • Strategic Initiatives
  • Takeda Pharmaceutical Company
    • Company Overview
    • Product Portfolio and Performance
    • Financial Performance
    • Technology Insights
    • Strategic Initiatives
  • Bayer AG
    • Company Overview
    • Product Portfolio and Performance
    • Financial Performance
    • Technology Insights
    • Strategic Initiatives
  • AbbVie Inc.
    • Company Overview
    • Product Portfolio and Performance
    • Financial Performance
    • Technology Insights
    • Strategic Initiatives
  • Merck & Co. Inc.
    • Company Overview
    • Product Portfolio and Performance
    • Financial Performance
    • Technology Insights
    • Strategic Initiatives
  • Bristol Myers Squibb
    • Company Overview
    • Product Portfolio and Performance
    • Financial Performance
    • Technology Insights
    • Strategic Initiatives

Frequently Asked Questions

The current market size of the Rare Disease Treatment industry is estimated to be $158.30 billion in 2023.

Increasing prevalence of rare diseases and rising investment in R&D

High cost of drug development and limited patient populations.

Injectables are the leading component segment in the Rare Disease Treatment Market.

Pfizer, Inc., PTC Therapeutics, AstraZeneca, Novartis AG, Takeda Pharmaceutical Company, Bayer AG, AbbVie Inc., Merck & Co. Inc are the major players operating in the Rare Disease Treatment Market.

The Rare Disease Treatment Market is expected to grow at a CAGR of 11.6% and reach a market size of $341.29 billion by 2030.